To Cure a Rose Foundation began in 2021 after Casey McPherson's daughter, Rose, was diagnosed with an ultra-rare genetic disease: HNRNPH2. Rose lost her ability to talk, walking is difficult, and she continues to retreat into a world away from her family. Rose and many others are on a clock, so we are racing to a cure. To learn more about the story, you can go HERE.

Currently, treatments for Rose, and the 200 million other children suffering from rare disease, cannot be developed by our current healthcare system due to lack of profit.
 

We are developing a genetic treatment for Rose's disease -- but Rose is just the beginning. We are building a pipeline to develop genetic treatments faster and more sustainably than ever before. 
 

Since beginning this journey to create a treatment for Rose's disease, we've helped fund a natural history study, started a lab, developed cell lines, created ASO (oligo) designs for a potential treatment, and are currently shortlisting the best ASOs for further testing at the Jackson Laboratory in Maine. The treatment is working in our cell lines and animal models...

As we get closer to a treatment, this program gets much more expensive.

We're at a pivotal moment at the foundation, and if we want to stay on track and get a treatment made, we need your help raising $100K online this year, with a total funding goal in 2024 for $500k. I know we can do this with your help! Every donation matters.

I want to see Rose play in the park, make friends, maybe even say Daddy again. But without a genetic treatment, she most likely never will. 

We envision a world where parents don't have to start foundations and grind for a treatment for their children. If we can treat Rose and create a sustainable pipeline for ultra rare disease drug development, then we can repeat the process for other children.

We envision a world where no parent has to hear there's nothing that can be done for their kids.

Make a donation, share our story, and help keep us in the fight for a cure.

To Cure A Rose Foundation is a 501(c)(3) non-profit organization.