We're at a crossroads, and we need your help!
 

Since beginning this journey to create a treatment for Rose's disease, we've funded a natural history study, started a lab, developed cell lines, created ASO (oligo) designs for a potential treatment, and are currently shortlisting the best ASOs for further testing at the Jackson Laboratory in Maine.

As we get closer to a treatment, this program gets much more expensive. We're at a pivotal moment at the foundation, and if we want to stay on track and get a treatment made, we need your help raising $700K by Fall 2023.

Make a donation, share our story, and help keep us in the fight for a cure!

Our Story
 

As a toddler, Rose McPherson was diagnosed with a rare genetic disease with no name, and no cure. To her father, Casey, it felt like a death sentence... until he spoke to hundreds of biotechs, foundations, and researchers. Casey learned:

We DO have the tools to cure Rose's disease (HNRNPH2), and many others.

We DON'T have the business models, pipelines, and financial support in place to do it.

To Cure A Rose Foundation was born to solve this problem for Rose and the 200m children that suffer from rare diseases. At the moment, 95% of them don't have any cures. This is an urgent health crisis for these forgotten children, and we aim to help fix it.

We start by saving Rose.